EFFICACY AND SAFETY OF ETRANACOGENE DEZAPARVOVEC IN ADULTS WITH SEVERE OR MODERATE-SEVERE HEMOPHILIA B: FIRST DATA FROM THE PHASE 3 HOPE-B GENE THERAPY TRIAL

Pipe, SW; Recht, M; Key, NS; Leebeek, FWG; Castaman, G; Lattimore, SU; van der Valk, P; Peerlinck, K; Coppens, M; O'Connell, N; Pasi, KJ; Kampmann, P; Meijer, K; von Drygalski, A; Young, G; Hermans, C; Astermark, J; Klamroth, R; Lemons, RS; Visweshwar, N; Crary, S; Kazmi, R; Symington, E; Escobar, MA; Gomez, E; Kruse-Jarres, R; Kotowski, A; Quon, D; Wang, M; Wheeler, AP; Sawyer, EK; Verweij, S; Colletta, V; Bajwa, N; Gut, R; Miesbach, W

EFFICACY AND SAFETY OF ETRANACOGENE DEZAPARVOVEC IN ADULTS WITH SEVERE OR MODERATE-SEVERE HEMOPHILIA B: FIRST DATA FROM THE PHASE 3 HOPE-B GENE THERAPY TRIAL

Author:

Pipe, SW

Recht, M ; Key, NS ; Leebeek, FWG ; Castaman, G ; Lattimore, SU ; van der Valk, P ; Peerlinck, K ; Coppens, M ; O'Connell, N ; Pasi, KJ ; Kampmann, P ; Meijer, K ; von Drygalski, A ; Young, G ; Hermans, C ; Astermark, J ; Klamroth, R ; Lemons, RS ; Visweshwar, N ; Crary, S ; Kazmi, R ; Symington, E ; Escobar, MA ; Gomez, E ; Kruse-Jarres, R ; Kotowski, A ; Quon, D ; Wang, M ; Wheeler, AP ; Sawyer, EK ; Verweij, S ; Colletta, V ; Bajwa, N ; Gut, R ; Miesbach, W

Keywords:

Science & Technology, Life Sciences & Biomedicine, Hematology, 1103 Clinical Sciences, Cardiovascular System & Hematology, 3202 Clinical sciences